Web10 mei 2024 · Ionis chief development officer Richard Geary told investors on their Q1 earnings call that they were cutting the Phase I/II CF program, known as Ionis-Enac-2.5-Rx, after a long-term toxicology in ... WebIonis Pharmaceuticals, Inc. is a biotechnology company based in Carlsbad, California, that specializes in discovering and developing RNA -targeted therapeutics.
IONIS PHARMACEUTICALS, INC. : koersdoel en …
Web28 feb. 2024 · Press Releases. Year. Mar 27, 2024. Ionis reports positive topline 66-week results of eplontersen Phase 3 study for patients with ATTRv-PN. Mar 22, 2024. Ionis announced FDA advisory committee voted unanimously for a potential accelerated approval of tofersen for SOD1-ALS. Mar 07, 2024. Web12 dec. 2024 · This move follows highly promising results from a Phase 1/2a clinical trial. The randomized, double-blind, placebo-controlled trial (NCT02519036) tested the safety and tolerability of several increasing doses of IONIS-HTTRx in Huntington’s disease patients.Pharmacokinetics (the movement of a drug within the body) and … eagle wisconsin diamond
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Web1 dec. 2024 · Detailed Description: This is a Phase 3, multi-center, double-blind, randomized, placebo-controlled study of donidalorsen in up to 84 participants. Participants will be randomized in a 2:1 ratio to Cohort A (donidalorsen or placebo every 4 weeks) or Cohort B (donidalorsen or placebo every 8 weeks), respectively. Web20 feb. 2024 · Ionis’ pipeline of antisense drugs is beginning to produce results – a separate alliance with Biogen resulted in development and approval of Spinraza (nusinersen), approved for spinal muscular... Web7 nov. 2024 · Safety, Tolerability, and Pharmacodynamics of IONIS-DGAT2Rx in Adult Patients With Type 2 Diabetes The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been evaluated by the U.S. Federal Government. Read our disclaimer for details. eagle wisconsin historical society